Inherited Retinal Disorders and Gene Therapy Quiz

What is a common characteristic of inherited retinal disorders?

• They only affect the elderly.

• They are caused by environmental factors.

• They improve over time.

• They are degenerative and worsen over time.

Which gene therapy has been approved for treating a specific retinal disorder in the U.S.?

• RetinaCare

• Luxturna

• GeneFix

• VisionAid

How does Luxturna work to treat retinal disorders?

• By delivering a functional copy of the gene

• By removing the faulty gene

• By using stem cells

• By altering the DNA sequence

What is a viral vector used for in gene therapy?

• To cause disease

• To deliver a functioning gene

• To remove damaged cells

• To enhance vision

Why is the retina considered an ideal target for gene therapy?

• It is resistant to treatment.

• It requires multiple injections.

• It is easily visualized and treated.

• It is difficult to access.